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2026

Accelerating Leigh syndrome drug discovery through deep learning screening in brain organoids.
Menacho, Carmen ORCID logoORCID: https://orcid.org/0000-0001-9754-6322, Okawa, Satoshi, Álvarez-Merz, Iris ORCID logoORCID: https://orcid.org/0000-0002-2585-1093, Wittich, Annika, Muñoz-Oreja, Mikel, Lisowski, Pawel ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Martín, Mario López, Pentimalli, Tancredi Massimo ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Zakin, Shiri, Thevandavakkam, Mathuravani, Jerred, Caleb, Lickfett, Selene ORCID logoORCID: https://orcid.org/0000-0002-3726-9551, Petersilie, Laura, Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Seibt, Annette, Herebian, Diran, Inak, Gizem, Brodesser, Susanne ORCID logoORCID: https://orcid.org/0000-0001-5631-0663, Zaliani, Andrea ORCID logoORCID: https://orcid.org/0000-0002-1740-8390, Mlody, Barbara ORCID logoORCID: https://orcid.org/0000-0001-5184-1772, Donnelly, Justin, Woleben, Kasey, Soriano, Francesc Xavier ORCID logoORCID: https://orcid.org/0000-0003-1678-7162, Fernandez-Checa, Jose C., Ventura, Natascia ORCID logoORCID: https://orcid.org/0000-0001-8718-4321, Cambridge, Sidney, Mayatepek, Ertan ORCID logoORCID: https://orcid.org/0000-0001-8460-3738, Spinazzola, Antonella ORCID logoORCID: https://orcid.org/0000-0003-4242-8091, Schuelke, Markus ORCID logoORCID: https://orcid.org/0000-0003-2824-3891, Rajewsky, Nikolaus ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Rossi, Andrea ORCID logoORCID: https://orcid.org/0000-0001-5863-6448, Peralvarez-Marin, Alex ORCID logoORCID: https://orcid.org/0000-0002-3457-0875, Distelmaier, Felix ORCID logoORCID: https://orcid.org/0000-0003-4304-7848, Perlstein, Ethan, Holt, Ian J., Puighermanal, Emma ORCID logoORCID: https://orcid.org/0000-0003-4271-9104, Pless, Ole ORCID logoORCID: https://orcid.org/0000-0002-1468-316X, Rose, Christine R. ORCID logoORCID: https://orcid.org/0000-0002-9684-3592, Del Sol, Antonio ORCID logoORCID: https://orcid.org/0000-0002-9926-617X and Prigione, Alessandro ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
Nature Communications 17 (1): 3570. 20 April 2026

MicroRNAs are required within a critical time window to define neural patterning during early human brain development.
Emmenegger, Lisa ORCID logoORCID: https://orcid.org/0000-0003-2165-7944, Cerda Jara, Cledi Alicia ORCID logoORCID: https://orcid.org/0000-0003-1783-5533, Ercolano, Matilde ORCID logoORCID: https://orcid.org/0009-0009-5966-2141, Loebert, Jaden, Morando, Nicolas, Bhaskar, Poojashree ORCID logoORCID: https://orcid.org/0009-0006-0027-7239, Legnini, Ivano ORCID logoORCID: https://orcid.org/0000-0002-8984-5215, Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290 and Rajewsky, Nikolaus ORCID logoORCID: https://orcid.org/0000-0002-4785-4332
bioRxiv : 2026.03.30.715268. 1 April 2026

Modelling cardiovascular diseases using human microphysiological systems.
Ribeiro, Quélia Ribeiro ORCID logoORCID: https://orcid.org/0009-0008-8104-0368, Lopes, Elizeth ORCID logoORCID: https://orcid.org/0000-0002-9837-5155, Ferreira, Inês S. ORCID logoORCID: https://orcid.org/0000-0002-5120-4869, Guerreiro Simões, Catarina ORCID logoORCID: https://orcid.org/0000-0003-1146-1737, Vital, Carlos Miguel ORCID logoORCID: https://orcid.org/0009-0008-0295-1455, Inácio, José Manuel ORCID logoORCID: https://orcid.org/0000-0002-9790-8335, Belo, José António ORCID logoORCID: https://orcid.org/0000-0001-7384-0949, Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Marques, André R.A. ORCID logoORCID: https://orcid.org/0000-0001-9674-3017 and Vieira, Otília V. ORCID logoORCID: https://orcid.org/0000-0003-4924-1780
BioChip Journal 20 (2): 236-269. April 2026

miRNA regulation in brain tissue space: the 3'UTR perspective.
Aigner, Denise ORCID logoORCID: https://orcid.org/0009-0001-0489-1010, Bartsch, Florian ORCID logoORCID: https://orcid.org/0000-0002-8285-9964, Bhaskar, Poojashree ORCID logoORCID: https://orcid.org/0009-0006-0027-7239, Emmenegger, Lisa ORCID logoORCID: https://orcid.org/0000-0003-2165-7944, Karaiskos, Nikos ORCID logoORCID: https://orcid.org/0000-0001-7771-3947, Rajewsky, Nikolaus ORCID logoORCID: https://orcid.org/0000-0002-4785-4332 and Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290
RNA 32 (4): 472-488. April 2026

Pluripotent stem-cell-based screening uncovers sildenafil as a mitochondrial disease therapy.
Zink, Annika ORCID logoORCID: https://orcid.org/0000-0002-8489-6339, Dai, Dao-Fu, Wittich, Annika, Henke, Marie-Thérèse ORCID logoORCID: https://orcid.org/0000-0001-6572-1667, Pedrotti, Giulia, Heiduschka, Sonja, Santamaria, Guillem, Pentimalli, Tancredi Massimo ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Brueser, Christian, Notopoulou, Sofia, Umar, Abdul Rahim, Zhaivoron, Aleksandra, Petersilie, Laura, Jerred, Caleb, Bergmans, Jesper, Neu, Louis Anton, Schumacher, Fabian, Keller-Findeisen, Jan, Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Stach, Daniel, Reinshagen, Jeanette, Haferkamp, Undine, Krieg, Kim, Zaliani, Andrea, Euro, Liliya, Di Donfrancesco, Alessia, Santanatoglia, Chiara, Cappellozza, Enrica, Suarez Cubero, Marta, Pavez-Giani, Mario, Bakumenko, Oleh, Meierhofer, David, Foley, Alan, Morales-Gonzalez, Susanne, Tolle, Isabella, Herebian, Diran, Bonesso, Daniele, Cecchetto, Giulia, Wong, Sakurako Nagumo, Moresco, Monica, Maresca, Alessandra, Decimo, Ilaria, De Sanctis, Francesco, Adamo, Annalisa, Adjobo-Hermans, Merel J.W., Duchi, Roberto, Barandalla, Maria, Scaglia, Marco, Perota, Andrea, Galli, Cesare, Kleuser, Burkhard, Cyganek, Lukas, Mühlhausen, Chris, Schlotawa, Lars, Tiranti, Valeria, Mayatepek, Ertan, Szabo, Ildiko, La Morgia, Chiara, Klopstock, Thomas, Carelli, Valerio, Distelmaier, Felix, Rossi, Andrea, Rajewsky, Nikolaus ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Ullah, Ghanim, Jakobs, Stefan, Rose, Christine R., Petrakis, Spyros, Edenhofer, Frank, Koopman, Werner J.H., Lisowski, Pawel ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Suomalainen, Anu, Brunetti, Dario, Del Sol, Antonio, Bottani, Emanuela, Pless, Ole ORCID logoORCID: https://orcid.org/0000-0002-1468-316X, Schuelke, Markus ORCID logoORCID: https://orcid.org/0000-0003-2824-3891 and Prigione, Alessandro ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
Cell 189 (6): 1656-1679.e42. 19 March 2026

2025

Staufen2 modulates the temporal dynamics of human neurogenesis in vitro.
Ganesh, Akshay Jaya ORCID logoORCID: https://orcid.org/0009-0005-7579-2924, Fernández-Moya, Sandra Maria ORCID logoORCID: https://orcid.org/0000-0002-5894-4296, Gutiérrez-Franco, Ana, Ferreira, Natalie Chaves ORCID logoORCID: https://orcid.org/0000-0002-0905-2670, Tur-Guasch, Rafael, Romero-Moya, Damia ORCID logoORCID: https://orcid.org/0000-0001-9947-3577, Giorgetti, Alessandra ORCID logoORCID: https://orcid.org/0000-0001-5803-3567, Mularoni, Loris ORCID logoORCID: https://orcid.org/0000-0001-7053-7717, Piwecka, Monika ORCID logoORCID: https://orcid.org/0000-0003-4104-6577, Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290 and Plass, Mireya ORCID logoORCID: https://orcid.org/0000-0002-9891-2723
bioRxiv : 2025.10.02.679988. 2 October 2025

Transcriptome-wide analysis of circRNA and RBP profiles and their molecular relevance for GBM.
Latowska-Łysiak, Julia, Zarębska, Zaneta, Sajek, Marcin P., Grabowska, Adriana, Buratin, Alessia, Głodowicz, Paweł, Misiorek, Julia O., Kuczyński, Konrad ORCID logoORCID: https://orcid.org/0000-0002-7664-1045, Bortoluzzi, Stefania, Żywicki, Marek, Kosiński, Jan G., Rybak-Wolf, Agnieszka ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Piestrzeniewicz, Rafał, Barciszewska, Anna M. and Rolle, Katarzyna ORCID logoORCID: https://orcid.org/0000-0002-4175-2490
Molecular Oncology 19 (8): 2270-2291. August 2025

UBE3C links ubiquitin signaling to epitranscriptomic control of cortical neurogenesis.
Borisova, Ekaterina, Cuthill, Katherine J. ORCID logoORCID: https://orcid.org/0000-0003-3328-3249, Dannenberg, Rike, Koch, Janina, Nowaczyk, Julius ORCID logoORCID: https://orcid.org/0009-0009-7068-4958, Schaub, Theres, Schwark, Manuela ORCID logoORCID: https://orcid.org/0009-0008-1711-457X, Kastelic, N., Kupryianchyk-Schultz, I. ORCID logoORCID: https://orcid.org/0009-0007-6442-4469, Kirchner, M. ORCID logoORCID: https://orcid.org/0000-0002-7049-534X, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Fokkens, T.J. ORCID logoORCID: https://orcid.org/0009-0005-4689-4024, Stein, F., Dietrich, C., Quedenau, C. ORCID logoORCID: https://orcid.org/0000-0002-6846-4915, Borodina, T. ORCID logoORCID: https://orcid.org/0000-0002-6978-016X, Schwefel, D. ORCID logoORCID: https://orcid.org/0000-0002-2945-0908, Conrad, T. ORCID logoORCID: https://orcid.org/0000-0001-5618-6295, Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Mertins, P. ORCID logoORCID: https://orcid.org/0000-0002-2245-528X, Haberkant, P. ORCID logoORCID: https://orcid.org/0000-0002-5608-9062, Lorenz, S. ORCID logoORCID: https://orcid.org/0000-0002-9639-2381, Brose, N. ORCID logoORCID: https://orcid.org/0000-0003-0938-8534, Kawabe, H. ORCID logoORCID: https://orcid.org/0000-0001-5650-8696, Tarabykin, V. ORCID logoORCID: https://orcid.org/0000-0001-8931-7263 and Ambrozkiewicz, M.C. ORCID logoORCID: https://orcid.org/0000-0001-5225-5230
bioRxiv : 2025.04.09.646620v2. 29 April 2025

2024

Mutant huntingtin impairs neurodevelopment in human brain organoids through CHCHD2-mediated neurometabolic failure.
Lisowski, P. ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Lickfett, S. ORCID logoORCID: https://orcid.org/0000-0002-3726-9551, Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Menacho, C. ORCID logoORCID: https://orcid.org/0000-0001-9754-6322, Le, S. ORCID logoORCID: https://orcid.org/0000-0002-7500-1759, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Notopoulou, S., Dykstra, W., Oehler, D. ORCID logoORCID: https://orcid.org/0000-0002-0435-4119, López-Calcerrada, S., Mlody, B. ORCID logoORCID: https://orcid.org/0000-0001-5184-1772, Otto, M. ORCID logoORCID: https://orcid.org/0009-0003-1919-5880, Wu, H., Richter, Y., Roth, P. ORCID logoORCID: https://orcid.org/0009-0006-8642-2993, Anand, R. ORCID logoORCID: https://orcid.org/0000-0001-7337-6007, Kulka, L.A.M. ORCID logoORCID: https://orcid.org/0009-0001-3640-3886, Meierhofer, D. ORCID logoORCID: https://orcid.org/0000-0002-0170-868X, Glazar, P. ORCID logoORCID: https://orcid.org/0000-0003-0842-0088, Legnini, I. ORCID logoORCID: https://orcid.org/0000-0002-8984-5215, Telugu, N.S. ORCID logoORCID: https://orcid.org/0000-0003-4509-7056, Hahn, T., Neuendorf, N., Miller, D.C. ORCID logoORCID: https://orcid.org/0000-0001-9852-677X, Böddrich, A. ORCID logoORCID: https://orcid.org/0000-0001-9118-050X, Polzin, A., Mayatepek, E. ORCID logoORCID: https://orcid.org/0000-0001-8460-3738, Diecke, S. ORCID logoORCID: https://orcid.org/0000-0002-5219-5992, Olzscha, H. ORCID logoORCID: https://orcid.org/0000-0002-1929-1384, Kirstein, J. ORCID logoORCID: https://orcid.org/0000-0003-4990-2497, Ugalde, C. ORCID logoORCID: https://orcid.org/0000-0002-9742-1877, Petrakis, S. ORCID logoORCID: https://orcid.org/0000-0001-9094-3480, Cambridge, S., Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Kühn, R. ORCID logoORCID: https://orcid.org/0000-0003-1694-9803, Wanker, E.E. ORCID logoORCID: https://orcid.org/0000-0001-8072-1630, Priller, J. ORCID logoORCID: https://orcid.org/0000-0001-7596-0979, Metzger, J.J. ORCID logoORCID: https://orcid.org/0000-0001-6813-4425 and Prigione, A. ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
Nature Communications 15 (1): 7027. 22 August 2024

3D spheroid and organoid models to study neuroinfection of RNA viruses.
Dos Reis, V.P., Cirksena, K., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Seeger, B., Herker, E. and Gerold, G.
Methods in Molecular Biology 2824 : 409-424. August 2024

Deep learning-driven neuromorphogenesis screenings identify repurposable drugs for mitochondrial disease.
Menacho, C., Okawa, S., Alvarez-Merz, I., Wittich, A., Muñoz-Oreja, M., Lisowski, P. ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Inak, G., Zakin, S., Thevandavakkam, M., Petersilie, L., Zaliani, A., Mlody, B. ORCID logoORCID: https://orcid.org/0000-0001-5184-1772, Seibt, A., Donnelly, J., Woleben, K., Fernandez-Checa, J., Herebian, D., Mayatepek, E., Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Spinazzola, A., Schuelke, M. ORCID logoORCID: https://orcid.org/0000-0003-2824-3891, Perlstein, E. ORCID logoORCID: https://orcid.org/0000-0002-4734-4391, Rossi, A., Distelmaier, F., Holt, I.J., Pless, O. ORCID logoORCID: https://orcid.org/0000-0002-1468-316X, Rose, C., Del Sol, A. and Prigione, A. ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
bioRxiv : 2024.07.08.602501. 12 July 2024

Generation and downstream analysis of single-cell and single-nuclei transcriptomes in brain organoids.
Wandres, M., Aigner, D. ORCID logoORCID: https://orcid.org/0009-0001-0489-1010, Kastelic, N., Boltengagen, A. ORCID logoORCID: https://orcid.org/0000-0002-8356-9766, Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290 and Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332
Journal of Visualized Experiments (205): e66225. 29 March 2024

2023

Spatiotemporal, optogenetic control of gene expression in organoids.
Legnini, I. ORCID logoORCID: https://orcid.org/0000-0002-8984-5215, Emmenegger, L. ORCID logoORCID: https://orcid.org/0000-0003-2165-7944, Zappulo, A., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Wurmus, R. ORCID logoORCID: https://orcid.org/0009-0003-0140-4189, Oliveras Martinez, A. ORCID logoORCID: https://orcid.org/0000-0002-5880-5245, Cerda Jara, C. ORCID logoORCID: https://orcid.org/0000-0003-1783-5533, Boltengagen, A. ORCID logoORCID: https://orcid.org/0000-0002-8356-9766, Hessler, T., Mastrobuoni, G. ORCID logoORCID: https://orcid.org/0000-0003-4509-1295, Kempa, S. ORCID logoORCID: https://orcid.org/0000-0002-0696-9299, Zinzen, R. ORCID logoORCID: https://orcid.org/0000-0002-8638-5102, Woehler, A. ORCID logoORCID: https://orcid.org/0000-0001-5157-9313 and Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332
Nature Methods 20 (10): 1544-1552. October 2023

A proteomics analysis of 5xFAD mouse brain regions reveals the lysosome-associated protein Arl8b as a candidate biomarker for Alzheimer's disease.
Boeddrich, A. ORCID logoORCID: https://orcid.org/0000-0001-9118-050X, Haenig, C. ORCID logoORCID: https://orcid.org/0000-0003-1973-7646, Neuendorf, N., Blanc, E. ORCID logoORCID: https://orcid.org/0000-0002-4369-0254, Ivanov, A. ORCID logoORCID: https://orcid.org/0000-0002-4824-1925, Kirchner, M. ORCID logoORCID: https://orcid.org/0000-0002-7049-534X, Schleumann, P., Bayraktaroğlu, I., Richter, M. ORCID logoORCID: https://orcid.org/0000-0002-5339-0781, Molenda, C.M. ORCID logoORCID: https://orcid.org/0000-0003-0771-405X, Sporbert, A. ORCID logoORCID: https://orcid.org/0000-0002-3738-1295, Zenkner, M., Schnoegl, S., Suenkel, C. ORCID logoORCID: https://orcid.org/0000-0002-5326-6043, Schneider, L.S., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Kochnowsky, B., Byrne, L.M., Wild, E.J., Nielsen, J.E., Dittmar, G. ORCID logoORCID: https://orcid.org/0000-0003-3647-8623, Peters, O. ORCID logoORCID: https://orcid.org/0000-0003-0568-2998, Beule, D. ORCID logoORCID: https://orcid.org/0000-0002-3284-0632 and Wanker, E.E. ORCID logoORCID: https://orcid.org/0000-0001-8072-1630
Genome Medicine 15 (1): 50. 20 July 2023

Modelling viral encephalitis caused by herpes simplex virus 1 infection in cerebral organoids.
Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Wyler, E. ORCID logoORCID: https://orcid.org/0000-0002-9884-1806, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Legnini, I. ORCID logoORCID: https://orcid.org/0000-0002-8984-5215, Oliveras Martinez, A. ORCID logoORCID: https://orcid.org/0000-0002-5880-5245, Glažar, P. ORCID logoORCID: https://orcid.org/0000-0003-0842-0088, Loewa, A. ORCID logoORCID: https://orcid.org/0000-0002-5551-731X, Kim, S.J. ORCID logoORCID: https://orcid.org/0000-0001-8357-0073, Kaufer, B.B. ORCID logoORCID: https://orcid.org/0000-0003-1328-2695, Woehler, A. ORCID logoORCID: https://orcid.org/0000-0001-5157-9313, Landthaler, M. ORCID logoORCID: https://orcid.org/0000-0002-1075-8734 and Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332
Nature Microbiology 8 (7): 1252-1266. July 2023

A circular RNA expressed from the FAT3 locus regulates neural development.
Seeler, S., Andersen, M.S., Sztanka-Toth, T. ORCID logoORCID: https://orcid.org/0000-0003-0185-5978, Rybiczka-Tešulov, M., van den Munkhof, M.H., Chang, C.C., Maimaitili, M., Venø, M.T., Hansen, T.B., Pasterkamp, R.J., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Denham, M., Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Kristensen, L.S. and Kjems, J. ORCID logoORCID: https://orcid.org/0000-0003-4128-9317
Molecular Neurobiology 60 (6): 3239–3260. June 2023

Single-cell and spatial transcriptomics: deciphering brain complexity in health and disease.
Piwecka, M. ORCID logoORCID: https://orcid.org/0000-0003-4104-6577, Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332 and Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290
Nature Reviews Neurology 19 (6): 346-362. June 2023

Sites of transcription initiation drive mRNA isoform selection.
Alfonso-Gonzalez, C., Legnini, I. ORCID logoORCID: https://orcid.org/0000-0002-8984-5215, Holec, S., Arrigoni, L., Ozbulut, H.C., Mateos, F., Koppstein, D., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Bönisch, U., Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332 and Hilgers, V.
Cell 186 (11): 2438-2455. 25 May 2023

2021

RNA dynamics in Alzheimer’s disease.
Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290 and Plass, M. ORCID logoORCID: https://orcid.org/0000-0002-9891-2723
Molecules 26 (17): 5113. 1 September 2021

Generation of human brain organoids for mitochondrial disease modeling.
Le, S., Petersilie, L., Inak, G., Menacho-Pando, C., Kafitz, K.W., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Rose, C.R. and Prigione, A. ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
Journal of Visualized Experiments (172): e62756. 21 June 2021

iPSC-derived 2D and 3D models of mitochondrial disease reveal early defects in neuronal morphogenesis and identify intervention strategies.
Inak, G., Rybak, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Lisowski, P. ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Karaiskos, N. ORCID logoORCID: https://orcid.org/0000-0001-7771-3947, Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Schuelke, M. ORCID logoORCID: https://orcid.org/0000-0003-2824-3891 and Prigione, A. ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
[Dataset] 20 April 2021

Defective metabolic programming impairs early neuronal morphogenesis in neural cultures and an organoid model of Leigh syndrome.
Inak, G., Rybak-Wolf, A. ORCID logoORCID: https://orcid.org/0000-0002-1192-5290, Lisowski, P. ORCID logoORCID: https://orcid.org/0000-0002-3634-1072, Pentimalli, T.M. ORCID logoORCID: https://orcid.org/0000-0002-8461-7918, Jüttner, R. ORCID logoORCID: https://orcid.org/0000-0003-3565-0698, Glažar, P. ORCID logoORCID: https://orcid.org/0000-0003-0842-0088, Uppal, K., Bottani, E. ORCID logoORCID: https://orcid.org/0000-0003-1217-8722, Brunetti, D. ORCID logoORCID: https://orcid.org/0000-0002-2740-9370, Secker, C. ORCID logoORCID: https://orcid.org/0000-0002-7222-536X, Zink, A. ORCID logoORCID: https://orcid.org/0000-0002-8489-6339, Meierhofer, D. ORCID logoORCID: https://orcid.org/0000-0002-0170-868X, Henke, M.T. ORCID logoORCID: https://orcid.org/0000-0001-6572-1667, Dey, M. ORCID logoORCID: https://orcid.org/0000-0002-9987-575X, Ciptasari, U. ORCID logoORCID: https://orcid.org/0000-0003-4577-3069, Mlody, B. ORCID logoORCID: https://orcid.org/0000-0001-5184-1772, Hahn, T., Berruezo-Llacuna, M., Karaiskos, N. ORCID logoORCID: https://orcid.org/0000-0001-7771-3947, Di Virgilio, M. ORCID logoORCID: https://orcid.org/0000-0001-5189-0793, Mayr, J.A. ORCID logoORCID: https://orcid.org/0000-0001-6970-336X, Wortmann, S.B., Priller, J. ORCID logoORCID: https://orcid.org/0000-0001-7596-0979, Gotthardt, M. ORCID logoORCID: https://orcid.org/0000-0003-1788-3172, Jones, D.P., Mayatepek, E., Stenzel, W., Diecke, S. ORCID logoORCID: https://orcid.org/0000-0002-5219-5992, Kühn, R. ORCID logoORCID: https://orcid.org/0000-0003-1694-9803, Wanker, E.E. ORCID logoORCID: https://orcid.org/0000-0001-8072-1630, Rajewsky, N. ORCID logoORCID: https://orcid.org/0000-0002-4785-4332, Schuelke, M. ORCID logoORCID: https://orcid.org/0000-0003-2824-3891 and Prigione, A. ORCID logoORCID: https://orcid.org/0000-0001-9457-1952
Nature Communications 12 (1): 1929. 26 March 2021

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