2015

Transposon-based, targeted ex vivo gene therapy to treat age-related macular degeneration (TargetAMD).
Thumann, G., Perdikomati-Dahmen, M., Izsvák, Z. ORCID: https://orcid.org/0000-0002-2053-2384, Ivics, Z. ORCID: https://orcid.org/0000-0002-7803-6658, Garcia Layana, A., Ronchetti, M., Petrovski, G., Scherman, D., Aranda, P., Pouillot, S., Binder, S., Johnen, S. and van den Berg, J.
Human Gene Therapy Clinical Development 26 (2): 97-100. 18 June 2015

2014

HEK293-based production platform for γ-retroviral (SIN-) vectors: application for safe and efficient transfer of COL7A1 cDNA.
Hennig, K., Raasch, L., Kolbe, C., Weidner, S., Leisegang, M. ORCID: https://orcid.org/0000-0003-3692-7142, Uckert, W., Titeux, M., Hovnanian, A., Kuehlcke, K. and Loew, R.
Human Gene Therapy Clinical Development 25 (4): 218-228. December 2014

2013

A seven-year storage report of good manufacturing practice-grade naked plasmid DNA: stability, topology, and in vitro/in vivo functional analysis.
Walther, W. ORCID: https://orcid.org/0000-0003-2884-0231, Schmeer, M., Kobelt, D. ORCID: https://orcid.org/0000-0002-9373-0648, Baier, R., Harder, A., Walhorn, V., Anselmetti, D., Aumann, J., Fichtner, I. and Schleef, M.
Human Gene Therapy Clinical Development 24 (4): 147-153. December 2013