Browse by Journal Title

2015

Transposon-based, targeted ex vivo gene therapy to treat age-related macular degeneration (TargetAMD).
Thumann, G. and Perdikomati-Dahmen, M. and Izsvák, Z. and Ivics, Z. and Garcia Layana, A. and Ronchetti, M. and Petrovski, G. and Scherman, D. and Aranda, P. and Pouillot, S. and Binder, S. and Johnen, S. and van den Berg, J.
Human Gene Therapy Clinical Development 26 (2): 97-100. 18 June 2015

2014

HEK293-based production platform for γ-retroviral (SIN-) vectors: application for safe and efficient transfer of COL7A1 cDNA.
Hennig, K. and Raasch, L. and Kolbe, C. and Weidner, S. and Leisegang, M. and Uckert, W. and Titeux, M. and Hovnanian, A. and Kuehlcke, K. and Loew, R.
Human Gene Therapy Clinical Development 25 (4): 218-228. December 2014

2013

A seven-year storage report of good manufacturing practice-grade naked plasmid DNA: stability, topology, and in vitro/in vivo functional analysis.
Walther, W. and Schmeer, M. and Kobelt, D. and Baier, R. and Harder, A. and Walhorn, V. and Anselmetti, D. and Aumann, J. and Fichtner, I. and Schleef, M.
Human Gene Therapy Clinical Development 24 (4): 147-153. December 2013